Research Awardees

Current CFRI-Funded Cystic Fibrosis Researchers

New Horizons Research

 

Stephen Aller, PhD
University of Alabama at Birmingham
Role of CFTR Arginine-933 in Folding, Gating and Potentiator Drug Binding

 

 

 

 

Steven Jonas, MD, PhD
University of California Los Angeles
Developing Nanotechnology-Enabled Gene Therapy Solutions to Correct CFTR Mutations in Airway Stem Cells: Toward a One-Time Cure for Cystic Fibrosis

 

 

 

Carlos Milla, MD

Carlos Milla, MD, Principal Investigator
Stanford University
Improving CF Airway Mucociliary Clearance: Toward Transition from Animals to Humans.

 

 

Kenichi Okuda, MD, PhD

Kenichi Okuda, MD, PhD, Principal Investigator
University of North Carolina at Chapel Hill
Pathways Maintaining Basal Mucin and CFTR-mediated Fluid Secretion in the Human Distal Airway 

 

 

 

Matthew Porteus, MD, PhD
Stanford Medical Center
Identifying Biomaterials that Enable the Transplantation of Gene Corrected Airway Stem Cells to Treat Cystic Fibrosis

 

Zachary M. Sellers, MD, PhD

 

Zachary Sellers, MD, PhD, Principal Investigator
Stanford University
Targeting IRBIT to Correct Bicarbonate Secretory Defects in Cystic Fibrosis

 

Elizabeth Nash Memorial Fellowship

Paul Bollyky, MD, PhD

Paul Bollyky, MD, PhD, Principal Investigator
Nina Pennetzdorfer, PhD, Postdoctoral Fellow
Stanford University
Targeting Bacterial Resistance to Phage Therapy in Cystic Fibrosis

 

 

Suzanne Fleiszig, PhD, Principal Investigator
Naren Gajenthra Kumar, PhD, Post-Doctoral Fellow
University of California Berkeley
Characterizing the Intracellular Diversification of Pseudomonas aeruginosa in Chronic Lung Infections

 

 

2019 – 2021 CFRI-Funded Cystic Fibrosis Researchers

New Horizons Research

Martina Gentzsch, PhD: Physiological Models of Cystic Fibrosis Airway Cultures that Mimic the In Vivo Environment for Therapeutic Testing; Principal Investigator, University of North Carolina at Chapel Hill

Lucas Hoffman, MD, PhD: Bacterial Community-Level Susceptibility Testing for CF Lung Infections; Principal Investigator, University of Washington, Seattle and Seattle Children’s Hospital

Elizabeth Kramer, MD, PhD: The Role of TGF in Driving Airway Hyperresponsiveness and Smooth Muscle Dysfunction in Cystic Fibrosis; Principal Investigator, Cincinnati Children’s Hospital Medical Center

Forest Rohwer, PhD: Development of tailocins against microbial infections in cystic fibrosis lungs; Principal Investigator, San Diego State University

Kenichi Okuda, MD, PhD: Regional regulation of CFTR and ionocyte expression in airways; Principal Investigator, University of North Carolina Chapel Hill

 

Elizabeth Nash Memorial Fellowship

Cynthia B. Silveira: Bacteriophage-Mediated Spread of Virulence Factors in Cystic Fibrosis Microbiomes; Postdoctoral Fellow, San Diego State University (Forest Rowher, PhD, Principal Investigator)

Keehoon Lee, PhD: A Multi-‘Omic Approach to Evaluate Concurrent Sinus and Pulmonary Disease in Cystic Fibrosis; Post-Doctoral Fellow, Northern Arizona University (Elizabeth Cope, PhD, Principal Investigator)